Safety and target engagement of an oral small-molecule sequestrant in adolescents with autism spectrum disorder: an open-label phase 1b/2a trial

A. Stewart Campbell, Brittany D. Needham, Christopher R. Meyer, Joanna Tan, Mary Conrad, Gregory M. Preston, Federico Bolognani, Srinivas G. Rao, Helen Heussler, Rebecca Griffith, Adam J. Guastella, Amy C. Janes, Blaise Frederick, David H. Donabedian & Sarkis K. Mazmanian